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Dwight Koeberl

Duke University, Durham NC

Dr Koeberl joined the Department of Pediatrics at Duke University in 1999. His research focuses on the development of new therapy for inherited metabolic disorders, especially for the glycogen storage diseases. He is currently developing drug and gene therapy for glycogen storage disease type I and for Pompe disease. He initiated a clinical trial of gene therapy for Pompe disease that is ongoing. His laboratory is developing gene editing with CRISPR/Cas9 for the glycogen storage diseases.

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