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Jennifer Adair
Fred Hutch Cancer Center
Helder Almeida Santos
University Medical Center Groningen
Douglas Anderson
University of Rochester School of Medicine and Dentistry
Ruiz Astigarraga
Galapagos
Stefano Benvenuti
Fondazione Telethon, Milan
Judith Breuer
UCL London
Marianne Carlon
KU Leuven
Vincenzo Cerullo
University of Helsinki
Cecilia Cotta-Ramusino
Tessera Therapeutics
Julio Delgado
IDIBAPS, University of Barcelona
Maria Eugenia Fernandez
Pietro Fratta
UCL Queen Square Institute of Neurology and the Francis Crick Institute
Gloria Gonzalez-Aseguinolaza
Cima, University of Navarra, Pamplona
Virginia Haurigot
Manel Juan
Hospital Clínic de Barcelona
Francisco Martín
GENYO, Granada
Luigi Naldini
SR Tiget, Milan
Philippe Parone
EsoBiotec
Matthias Renner
Paul-Ehrlich-Institut (PEI)
Juan Roberto Rodriguez Madoz
Jan Schrooten
Antleron
Cristian Smerdou
Zuzana Spacirova
Junta de Andalucia, Granada
Simao Teixera da Rocha
University of Lisbon
Xavier Trepat
IBEC, Barcelona
Anna Villa
SR-Tiget, Milan
Nerea Zabaleta
CIMA, University of Navarra
Oumeya Adjali
INSERM UMR 1089, Nantes
Maria Alonso
University of Santiago de Compostela
Caroline Arber
University of Lausanne
Alberto Auricchio
Tigem, Naples
Barbara Bonamassa
AIFA
Li-An Brown
UCL Great Ormond Street Institute of Child Health.
Gabriele Casirati
Boston Children’s Hospital and Dana-Farber Cancer Institute
Lisa Chakrabarti
Institut Pasteur, Paris
Jay Daniels
Northwestern
Ben Deverman
Broad Institute of MIT and Harvard
Giuliana Ferrari
SR-Tiget
Anne Galy
ART-TG - Inserm US35
Steven Gray
UT Southwestern
Zoltan Ivics
Paul Ehrlich Institute, Langen
Paschalia Koufokotsiou
European Commission
Alan Melcher
The Institute of Cancer Research, London,
Elizabeth Ng
Murdoch Children's Research Institute, Melbourne
Kinnari Patel
Rocket Pharma
Katy Rezvani
University of Texas MD Anderson Cancer Center
Giuseppe Ronzitti
Genethon and UMR_951, Evry
Birgit Schultes
Intellia Therapeutics
Yeowon Sohn
Sungkyunkwan University,
Mario Squadrito
SR- Tiget, Milan
Francesco Testa
University of Campania Luigi Vanvitelli, Naples
Cesar Trigueros Fernandez
Viralgen
Elizabeth White
Orphan Therapeutics Accelerator,
Wolfram Zimmermann
Universität Göttingen
Alessandro Aiuti
Luis Alvarez-Vallina
Spanish National Cancer Research Centre (CNIO), Madrid
Manuel Arellano
Platform of Patient Organizations
Christopher Baum
BIH, Charité, Berlin
Melissa Bonner
nChroma Bio
Juan Bueren
CIEMAT/Ciberer, Madrid
Toni Cathomen
University of Freiburg
Jeffrey Chamberlain
University of Washington
Olivier Danos
RegenX bio
George Diaz
iECURE, Philadelphia
Terence Flotte
UMass Chan Medical School
Lindsey George
University of Pennsylvania
Stefano Gritti
UCL Institute of Child Health, London
Juan Carlos Izpisúa Belmonte
San Diego Institute of Science.
Sandra Le Quellec
CSL Behring
Michela Milani
Karen Oprych
Great Ormond Street Hospital, London
Pasquale Piccolo
Paula Rio
Ciemat/Ciberer, Madrid
Claudia Rössig
University Children´s Hospital Muenster
Jonathan Schwartz
Erik Sontheimer
University of Massachusetts Chan Medical School
Didier Stainier
Max Planck Institute for Heart and Lung Research, Bad Nauheim
Marija Tomovic
TIGEM, Naples
Fleur van Dijk
Imperial College London
James Wilson
Gemma Biotherapeutics
Ramon Alemany
IDIBELL, Barcelona
Daniel Anderson
Massachusetts Institute of Technology
Aravind Asokan
Duke University
Jon Beaman
MHRA
Claire Booth
UCL
Hildegard Büning
Hannover Medical School
Anna Cereseto
University of Trento
Yvonne Chen
UCLA
Beverly Davidson
Children’s Hospital of Philadelphia and University of Pennsylvania
Isabel Fariñas
University of Valencia
Graham Foster
Queens University London
Paul Gissen
UCLondon
Sonia Guedan
IDIBAPS, Barcelona
Lukas Jeker
University of Basel
Juliette Lemoine
Institut Imagine, Paris
Kiran Musunuru
Perelman School of Medicine, University of Pennsylvania
Sung-Yun Pai
National Cancer Institute, National Institutes of Health
Ellen Reisinger
ENT Clinic, Tübingen
Sandra Rodriguez
Axel Schambach
Robin Shattock
Elena Sotillo
Stanford University
Lorenz Studer
Memorial Sloan Kettering Cancer Center
Ivana Trapani
Els Verhoeyen
EVIR, INSERM U758, Lyon; C3M, INSERM U1065, Nice
Paul Yang
Portland, Oregon