08:30-09:00 | Registration Foyer
Registration

09:00-10:45 | Meeting Room 1

Education 1a: Delivery Tools – from first generation vectors to advanced biological nanoparticles

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09:00-09:05 Hildegard Büning, Hannover Medical School 
Welcome
 

09:05-09:30  EDU01: Luk Vandenberghe, The Broad Institute of Harvard and MIT
Non-integrating viral vectors (AAV and AdV)

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09:30-09:55  EDU02: Anne Galy, ART-TG – Inserm US35
Integrating viral vectors (gamma retroviral vectors, lentiviral vectors, etc)

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09:55-10:20  EDU03: Dan Peer, University of Tel Aviv
Non-viral vectors (LNP technology)

10:20- 10-45  EDU04: Els Verhoeyen, EVIR, INSERM U758, Lyon; C3M, INSERM U1065, Nice
Strategies for tailoring vectors into cell type selective biological nanoparticles

09:00-10:45 | Meeting Room 2
Session 1b: Gene Therapy for Monogenic Diseases: Concepts – Applications – Challenges and possible solutions

09:00-09:05 Ivana Trapani, Tigem Naples

Welcome and chairs
 

09:05-09:30  EDU05: Claire Booth, University College London

Ex vivo gene therapy strategies – focus on PID
 

09:30-09:55  EDU06: Maria Ester Bernardo, SR-Tiget, Milan

​Ex vivo gene therapy strategies – focus on lysosomal storage diseases

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09:55-10:20  EDU07: Nathalie Cartier, AskBio, Paris
In vivo gene therapy strategies – focus on CNS

10:20-10:45  EDU08: Thierry VandenDriesche, VUB, Brussels
In vivo gene therapy strategies – focus on muscle

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10:45-11:15 | Registration Foyer / Forum

Coffee Break

11:15-12:55 | Meeting Room 1

Session 2a: Genome Editing and beyond

​Chair: HIldegard Büning

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11:15-11:40  EDU09: Julian Grünewald, TUM, Munich

Genome Editing – basic insights

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​11:40-12:05  EDU10: Angelo Lombardo, SR-Tiget, Milan

​Next generation genome editing strategies and tools

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12:05-12:30  EDU11: Matthew Porteus, Stanford University
Challenges and Promises in Genome Editing – insights from pre-clinical and clinical applications

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12:30-12:55  EDU12: Axel Schambach, Hannover Medical School

Gene addition vs Genome Editing – pros and cons

11:15-12:30 | Meeting Room 2

Session 2b: Cancer – novel therapy concepts fighting an old foe

​Chair: Anne Galy

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11:15-11:40  EDU13: Vincenzo Cerullo, University of Helsinki

​Oncolytic virus, as it is now!

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11:40-12:05  EDU014: Eliana Ruggiero, Universita Via-Salute San Raffaele, Milan

​CAR T cells, rTCR T cells and beyond

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12:05-12:30  EDU015: Bernhard Gentner, Ludwig Institute for Cancer Research, Lausanne

​Novel targets in cancer gene therapy

12:30-13:00 | Meeting Room 2

Session 2c: From preclinical development to clinics – the long path to translation

​Chair: Anne Galy

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12:30-13:00  EDU16: Amit Nathwani, University College London

​From preclinical development to clinics – the long path to translation

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13:00-14:00 | Forum and Registration Foyer

Lunch